Genetix Biotherapeutics

Medical Director

• Serve as a subject matter expert and team leader for programs/indications supporting our gene therapy portfolio.
• Lead efforts to bridge clinical science and commercial efforts by ensuring strategic alignment across various internal and external functions.
• Focus on peer-to-peer interactions, the development and execution of advisory boards, KOL advocacy, congress presence, and medical symposia.
• Provide structured feedback to internal teams relative to actionable field insights and advance data generation efforts.
• Develop and execute Medical Affairs strategy across sickle cell disease (SCD) and transfusion dependent thalassemia (TDT).
• Build external relationships to provide scientific and clinical information on therapies to key HCP and bring actionable insights from KOL and treating physicians.
• Engage with industry experts to garner support for scientific messages, clinical research, and product value.
• Offer medical expertise and input to cross-functional teams including commercial, clinical, operations, payor, and advocacy.
• Support the creation of evidence-based content that enhances patient-provider communication.
• Maintain compliance with applicable company policies and regulations.

Regional Medical Director, Gene Therapy

Director

• Provide high-touch, education, support & resources to patients and caregivers regarding the gene therapy treatment process, including pre-treatment considerations, treatment day logistics, and post-treatment expectations.
• Educate the patient on their gene therapy coverage based on their benefits and the steps needed to gain prior authorization to ensure understanding of the process for access.
• Assess patient and caregiver needs, tailoring resources and education to ensure understanding, confidence, and support.
• Serve as a trusted point of contact for patients, ensuring questions are answered in a compassionate and compliant manner.
• Guide patients through the treatment journey, coordinating support services such as travel, lodging, reimbursement, and offering connection to resources.
• Identify potential barriers to treatment and implement proactive strategies to resolve access challenges in collaboration with cross-functional partners.
• Monitor patient milestones and adherence to treatment timelines, ensuring delivery of high-quality and timely support.
• Educate internal and external stakeholders on the program to drive awareness.
• Work with Qualified Treatment Centers (QTCs) to monitor patient status and facilitate patient support.
• Partners with QTCs, healthcare providers, and advocacy organizations to enhance patient and caregiver education, increase awareness of program services, and support treatment readiness.
• Represent Patient Services at community-based organization (CBO) events, patient advocacy conferences, and industry meetings.
• Gather insights from QTC visits, CBO interactions, and conference attendance to inform program design, messaging, and outreach strategy.
• Communicate key insights and patient trends back to internal stakeholders to continuously refine engagement approaches and optimize program design.
• Contribute to the design and implementation of patient support initiatives, work instructions, patient-facing resources, and best practices.
• Utilize data, analytics, and patient feedback to identify opportunities for program improvement and drive excellence.

Regional Medical Director, Gene Therapy

Associate Director, Patient Navigator